Muscular dystrophy cured with CRISPR gene therapy which replaced dysfunctional genes in all muscles in adult mice.

www.eurekalert.org

Muscular dystrophy was cured in adult mice using a new gene-editing technique called CRISPR/AAV which replaced the dysfunctional dystrophin gene a with functional one in all muscle cells and increased muscle strength. The breakthrough here is that the CRISPR/AAV was able to reach all muscles, including in the heart, after being injected into an adult mouse’s bloodstream. Duchenne muscular dystrophy affects 1 in 5,000 males and most are wheelchair-bound by age 10 and don’t live beyond their 20s or early 30s.

Unlock the Science Digest — our exclusive biweekly newsletter featuring the latest scientific discoveries, concise summaries, and Rhonda's expert commentary. Available only to FoundMyFitness Premium Members.

Choose a monthly subscription in
any eligible amount
Already have an account? Log in
Monthly
Save 20%
Yearly